First-Ever Custom CRISPR Therapy Saves Infant With Deadly Genetic Disorder
A pivotal aesculapian milepost has been reached . For the first time ever , researchers have used a personalized CRISPR - based gene therapy to treat an infant ’s rarefied and life - threatening illness . physician at the Children ’s Hospital of Philadelphia ( CHOP ) and Penn Medicine detail their achievement in a studypublishedThursday in the New England Journal of Medicine . The handle child , identify KJ , was born with a metabolic disorder known to pop up to 50 % of children in their infancy ....